CRISPR therapy STX-1150 could replace daily cholesterol pills with a single dose, reducing LDL by 50% for 18+ months using ...

Caffeine could act as an on-off switch for gene and cell therapies, giving doctors more precise control over powerful ...

Gene-editing tools like CRISPR have unlocked new treatments for previously uncurable diseases. Now, researchers at the ...

A new CRISPR-based one-off procedure that lowers "bad" cholesterol has been approved to enter Phase I human trial. If ...

For decades, high cholesterol has meant a lifetime of daily pills, repeat blood tests and constant reminders that the biggest ...

Intellia is instituting new safeguards following the death of a study participant that led regulators to pause two trials in ...

Gene-editing tools like CRISPR have unlocked new treatments for previously uncurable diseases. Now, researchers at the University of British Columbia ...

Last year, a ten-month-old baby in the US was the first person in the world to have their rare genetic disease effectively ...

Dr. Hong Li, professor in Van Andel Institute’s Department of Structural Biology, leverages CRISPR, cryo-EM and other leading-edge technologies to explore the mechanisms underlying RNA-mediated ...

After a patient safety signal and then death, the FDA in October 2025 placed holds on two of the company’s CRISPR programs for hereditary transthyretin amyloidosis.

Genetic disorders occur due to alterations in the primary genetic material, deoxyribonucleic acid (DNA), of an organism.

CRISPR gene editing has transitioned from a laboratory curiosity to a cornerstone of modern biotechnology, revolutionizing our approach to genetic diseases, including Charcot-Marie-Tooth (CMT) disease ...